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ReviewAdvances in therapy2026

Study Designs and Crafting Endpoints for Gene Therapy Development Programs in Rare Disease: A Narrative Review.

Lindsey T Murray et al.PubMed ↗Full text ↗Publisher ↗

No numbers read from the abstract.

2 papers cite it

2026
this papercites it
Full record →Abstract, authors, funding and every citing paper · PMID 41269517