ArticleGene therapy2025
Gene editing for Spinocerebellar ataxia type 3 taking advantage of the human ATXN3L paralog as replacement gene.
Margareta Rybarikova et al.PubMed ↗Full text ↗Publisher ↗
No numbers read from the abstract.
ArticleGene therapy2025
Margareta Rybarikova et al.PubMed ↗Full text ↗Publisher ↗
No numbers read from the abstract.