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Observational studyMuscle & nerve2025

Risdiplam in Adult Patients With 5q Spinal Muscular Atrophy: A Single-Center Longitudinal Study.

Maria Gavriilaki et al.PubMed ↗Full text ↗Publisher ↗

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9 papers cite it

2025
2026
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Full record →Abstract, authors, funding and every citing paper · PMID 39722647