ArticleMolecular therapy. Advances2026
Next generation AAV-F capsid gene therapy rescues disease pathology in a model of pyruvate dehydrogenase complex deficiency.
Anna Keegan et al.PubMed ↗Full text ↗Publisher ↗
No numbers read from the abstract.
ArticleMolecular therapy. Advances2026
Anna Keegan et al.PubMed ↗Full text ↗Publisher ↗
No numbers read from the abstract.