Evidence map›Paper›PMID 42398968›Full record

ArticleJournal for immunotherapy of cancer2026

Circumventing Ewing sarcoma tumor microenvironment resistance by IL1RAP CAR-modified TGFβ1-imprinted natural killer cells in combination with IL-15 agonist and anti-GD2 antibody.

Wen Luo, Hai-Feng Zhang, Wei Li, Changxin Xu, Hongwen Zhu, Marcelo Pereira, Justin Lyberger, Shiori Eguchi, Yanling Liao, Jeremy M Rosenblum and 5 more

Abstract read
In one paragraph

Article in Journal for immunotherapy of cancer, 2026. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Not yet cited in PubMed.

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0citing papers in PubMed
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1 · What the graph read from it

What it found

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The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

0 citing papers in PubMed.

No citing paper in PubMed yet.

4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

15 authors.

Wen LuoPediatrics, New York Medical College, Valhalla, NY, USA mitchell_cairo@nymc.edu wen_luo@nymc.edu.
Hai-Feng ZhangMolecular Oncology, British Columbia Cancer Research Institute, Vancouver, BC, Canada.
Wei LiDepartment of Medicine, University of Pittsburgh School of Medicine, Pittsburgh, Pennsylvania, USA.
Changxin XuJames J. Peters Veterans Affairs Medical Center, Bronx, NY, USA.
Hongwen ZhuPediatrics, New York Medical College, Valhalla, NY, USA.
Marcelo PereiraNationwide Children's Hospital, Columbus, OH, USA.ORCID http://orcid.org/0000-0001-7069-5328
Justin LybergerInternal Medicine, Division Of Hematology, The Ohio State University, Columbus, Ohio, USA.
Shiori EguchiPediatrics, New York Medical College, Valhalla, NY, USA.ORCID http://orcid.org/0000-0002-9333-8208
Yanling LiaoPediatrics, New York Medical College, Valhalla, NY, USA.
Jeremy M RosenblumPediatrics, New York Medical College, Valhalla, NY, USA.
Mario MarcondesNektar Therapeutics, San Francisco, California, USA.
Gregory BehbehaniInternal Medicine, Division Of Hematology, The Ohio State University, Columbus, Ohio, USA.
Poul H SorensenMolecular Oncology, British Columbia Cancer Research Institute, Vancouver, BC, Canada.
Dean LeeNationwide Children's Hospital, Columbus, OH, USA.ORCID http://orcid.org/0000-0001-6693-5392
Mitchell S CairoPediatrics, New York Medical College, Valhalla, NY, USA mitchell_cairo@nymc.edu wen_luo@nymc.edu.ORCID http://orcid.org/0000-0002-2075-434X

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

backgroundThe prognosis of patients with metastatic/relapsed/refractory Ewing sarcoma (ES) is dismal. Natural killer (NK) cells are highly cytotoxic to ES but limited by resistance within the ES tumor microenvironment (TME). Here we sought to overcome ES resistance to NK cells by a combinatorial immunotherapy approach simultaneously enabling NK tumor-specific-targeting via chimeric antigen receptor (CAR) against a novel ES target interleukin-1 receptor accessory protein (IL1RAP), circumventing transforming growth factor beta (TGFβ)-mediated NK immunosuppression by TGFβ1-imprinting, increasing NK cell antibody-dependent cellular cytotoxicity (ADCC) via an anti-GD2 antibody dinutuximab, and improving NK cell persistence and ADCC by an IL-15 agonist, NKTR-255.

methodsPeripheral blood mononuclear cells were expanded into NK and TGFβ1-imprinted-NK (imNK) cells using antigen-presenting feeder cells co-expressing IL-21 and 4-1 BBL. Anti-IL1RAP-CAR messenger RNA was electroporated into NK or imNK cells. In vitro cytotoxicity assays were performed to investigate the efficacy of anti-IL1RAP-CAR-NK/imNK cell alone or combined with NKTR-255 and/or dinutuximab against ES cells. Xenograft mouse models of ES were used to investigate the antitumor efficacy of the combinatorial CAR-NK/imNK cell therapy against ES in vivo. Single-cell RNA sequencing and mass cytometry analyses of cells from xenograft tumors were performed to identify mechanisms of response/resistance to this combinatorial immunotherapy.

resultsWe found that anti-IL1RAP-CAR-NK cells significantly and specifically enhanced NK cytotoxicity in vitro and decreased tumor growth and lung metastasis in vivo against IL1RAP+ES. TGFβ1-imprinting significantly enhanced in vitro cytotoxicity and tumor infiltration of CAR-NK cells, leading to significantly reduced tumor growth and improved animal survival in the ES orthotopic mouse model. Compared with single agent or double combinations, the triple combination of imprinted-CAR-NK (CAR-imNK) cells and NKTR-255 with dinutuximab had superior antitumor efficacy against IL1RAP+GD2+ ES. Mechanistic studies on single cells from the xenograft tumors revealed increased apoptosis of ES cells, upregulated expression of ligands to NK inhibitory receptors on ES cells, and enhanced mouse macrophage migration in the ES TME in response to the CAR-imNK+NKTR-255+dinutuximab therapy.

conclusionsOur preclinical data demonstrate that combinatorial innate immunotherapy leveraging tumor-targeting TGFβ1-imprinted IL1RAP-CAR-NK cells combined with an IL-15 agonist and an anti-GD2 antibody is a promising novel therapeutic strategy for targeting metastatic/relapsed/refractory ES.

Indexed as

Antibodies, MonoclonalInterleukin-15Killer Cells, NaturalReceptors, Chimeric AntigenSarcoma, EwingTransforming Growth Factor beta1AnimalsCell Line, TumorCombined Antibody TherapeuticsFemaleGangliosidesHumansMiceTumor MicroenvironmentXenograft Model Antitumor AssaysAntibodies, MonoclonalCombined Antibody Therapeuticsganglioside, GD2GangliosidesIL15 protein, humanInterleukin-15Receptors, Chimeric AntigenTransforming Growth Factor beta1Bone CancerChimeric antigen receptor - CARCombination therapyImmunotherapyNatural killer - NK

Identifiers

PMID42398968
PMCPMC13343034

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Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the OpenQuestion graph.