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ArticleEuropean journal of neurology2026

Deep Phenotyping of F64L Mutation in a Multicentric Cohort of Patisiran-Treated Hereditary Transthyretin Amyloidosis Patients (Patisiranitaly).

Marco Ceccanti et al.PubMed ↗Full text ↗Publisher ↗

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2026
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Full record →Abstract, authors, funding and every citing paper · PMID 42226514