Evidence map›Paper›PMID 41947145›Full record

ArticleOrphanet journal of rare diseases2026

TrialR: critical enablers and the need for reusable Rare Disease Clinical Trial infrastructure in Western Australia.

Bradley MacDonald, Maddison Burmaz, Sue Baker, Kaila Stevens, Amanda Newell, Gareth Baynam

Abstract readLetter
In one paragraph

Article in Orphanet journal of rare diseases, 2026. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Not yet cited in PubMed.

0numbers the graph read from it
0cells of the map it votes in
0citing papers in PubMed
–field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

0 citing papers in PubMed.

No citing paper in PubMed yet.

4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

6 authors.

Bradley MacDonaldRare Care Centre, Perth Children's Hospital, 15 Hospital Ave, Nedlands, WA, 6008, Australia. bradley.macdonald@uwa.edu.au.ORCID http://orcid.org/0000-0003-2812-0744
Maddison BurmazRare Care Centre, Perth Children's Hospital, 15 Hospital Ave, Nedlands, WA, 6008, Australia.
Sue BakerRare Care Centre, Perth Children's Hospital, 15 Hospital Ave, Nedlands, WA, 6008, Australia.
Kaila StevensRare Care Centre, Perth Children's Hospital, 15 Hospital Ave, Nedlands, WA, 6008, Australia.
Amanda NewellRare Care Centre, Perth Children's Hospital, 15 Hospital Ave, Nedlands, WA, 6008, Australia.
Gareth BaynamRare Care Centre, Perth Children's Hospital, 15 Hospital Ave, Nedlands, WA, 6008, Australia.

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

PubMed holds no abstract for this paper.

Indexed as

Adaptive platform clinical trialsCritical enablersRare diseasesTrial access

Identifiers

PMID41947145
PMCPMC13059355

What OpenQuestion holds

Textmetadata
LicenceCC BY
Read underepoch 390

Registered trials

None linked

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the OpenQuestion graph.