TrialJournal of inherited metabolic disease2026

Pharmacodynamics, Efficacy, and Safety of Intraputaminal Eladocagene Exuparvovec Administered to Pediatric Patients With Aromatic L-Amino Acid Decarboxylase Deficiency Using an MR-Compatible Cannula: 48 Weeks of Follow-Up.

Daniel J Curry et al.PubMed ↗Full text ↗Publisher ↗

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