Evidence map›Paper›PMID 41668809›Full record

ArticleFrontiers in pharmacology2025

Designing integrated early-phase protocols to reduce substantial modifications, including considerations for patient cohorts - a multi-stakeholder consensus view for a practical approach in Germany.

R Schultz-Heienbrok, S Baumann, R Böhm, A Bonertz, K Breithaupt-Groegler, U Buckpesch-Heberer, M Coenen, K Erb-Zohar, N Faisst, G Grass and 9 more

Erratum issuedAbstract read
In one paragraph

Article in Frontiers in pharmacology, 2025. The graph could read no effect estimate from its abstract, so it casts no vote on the map. An erratum has been issued. Not yet cited in PubMed.

0numbers the graph read from it
0cells of the map it votes in
0citing papers in PubMed
–field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

0 citing papers in PubMed.

No citing paper in PubMed yet.

4 · The record

Corrections and comments

5 · Who and what money

Authors and funding

19 authors.

R Schultz-HeienbrokCharité Research Organisation GmbH, Berlin, Germany.
S BaumannCRS Clinical Research Services Management, Berlin, Germany.
R BöhmSocraTec R&D, Oberursel, Germany.
A BonertzPaul-Ehrlich-Institut, Langen, Germany.
K Breithaupt-GroeglerConsultant Clinical Pharmacology, Frankfurt, Germany.
U Buckpesch-HebererPaul-Ehrlich-Institut, Langen, Germany.
M CoenenInstitute of Clinical Chemistry and Clinical Pharmacology, University Hospital Bonn, Bonn, Germany.
K Erb-ZoharClinphase, Schotten, Germany.
N FaisstDr. Falk Pharma GmbH, Freiburg, Germany.
G GrassSpezialisierte Ethikkommission für besondere Verfahren, Bonn, Germany.
J HöchelBayer AG, Berlin, Germany.
A KovarSanofi, Frankfurt, Germany.
A MuehlenbroichNovartis, Basel, Switzerland.
J RengelshausenUniklinik RWTH Aachen, Aachen, Germany.
C RiedelBundesinstitut für Arzneimittel und Medizinprodukte, Bonn, Germany.
B SchugSocraTec R&D, Oberursel, Germany.
T SudhopBundesinstitut für Arzneimittel und Medizinprodukte, Bonn, Germany.
A WarnkeSocraTec R&D, Oberursel, Germany.
B ZiegeleInstitute of Clinical Chemistry and Clinical Pharmacology, University Hospital Bonn, Bonn, Germany.

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

• Frequent substantial modifications for initiating new trial parts slow down development and reduce transparency. • Combining healthy volunteers and patients in a single early-phase trial raises safety, feasibility, and regulatory concerns. • A multi-stakeholder consensus in Germany identified regulatory pathways to enable seamless transitions within integrated protocols for non-ATMP (advanced therapy medicinal product), non-oncology trials. • The EMA FIH (first-in-human) guideline supports predefined transitions if scope, safety thresholds, and decision rules are clearly described. • The German guardrail concept clarifies when transitions do not require a substantial modification, enhancing planning certainty. • Actionable recommendations are provided on protocol design, decision criteria, and governance structures to enable early inclusion of patients without compromising safety or compliance. • First positive experience has been gained with the presented framework in Germany.

Indexed as

clinical trialscomplex trial designfirst-in-humanintegrated protocolsinvestigational medicinal productsubstantial modification

Identifiers

PMID41668809
PMCPMC12883952

What OpenQuestion holds

Textmetadata
LicenceCC BY
Read underepoch 390

Registered trials

None linked

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the OpenQuestion graph.