Evidence map›Paper›PMID 41598837›Full record

ArticleJournal of clinical medicine2026

Using Patient Feedback to Improve Treatment Outcomes for Patients with Congenital Dyserythropoietic Anaemia Type I Receiving Interferon Therapy.

Karl Frey, Sanja Brolih, Caroline Scott, Nicholas Fordham, Sam Burrows, Nyree Cole, Karen Deem, Christopher Jenkins, Melanie Proven, Christian Babbs and 1 more

Abstract read
PubMed Full text at PMC Publisher
In one paragraph

Article in Journal of clinical medicine, 2026. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Not yet cited in PubMed.

0numbers the graph read from it
0cells of the map it votes in
0citing papers in PubMed
–field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

0 citing papers in PubMed.

No citing paper in PubMed yet.

4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

11 authors.

Karl FreyDepartment of Haematology, Oxford University Hospitals NHS Trust, Churchill Hospital, Old Road, Headington, Oxford OX3 7LE, UK.
Sanja BrolihCentre for Medicines Discovery, University of Oxford, Oxford OX3 7FZ, UK.ORCID 0000-0001-6192-9866
Caroline ScottMRC Weatherall Institute of Molecular Medicine, University of Oxford, John Radcliffe Hospital, Oxford OX3 9DU, UK.
Nicholas FordhamEvalina Children's Hospital, St Thomas Hospital, London SE1 7EH, UK.
Sam BurrowsDepartment of Haematology, University Hospitals Plymouth NHS Trust, Derriford Road, Plymouth PL6 8DH, UK.
Nyree ColeEpsom and St Helier University Hospitals NHS Trust, Sutton SM5 1AA, UK.
Karen DeemPortsmouth University Hospitals NHS Trust, Portsmouth PO6 3LY, UK.
Christopher JenkinsAneurin Bevan University Health Board, Newport NP11 5GH, UK.ORCID 0009-0005-5743-5894
Melanie ProvenRegional Genetic Laboratory, Oxford University Hospitals NHS Trust, Churchill Hospital, Old Road, Headington, Oxford OX3 7LE, UK.ORCID 0009-0008-2251-2257
Christian BabbsMRC Weatherall Institute of Molecular Medicine, University of Oxford, John Radcliffe Hospital, Oxford OX3 9DU, UK.ORCID 0000-0002-1898-5878
Noemi Bernadette Alice RoyDepartment of Haematology, Oxford University Hospitals NHS Trust, Churchill Hospital, Old Road, Headington, Oxford OX3 7LE, UK.

Funding

Congenital Anaemia Network NA
6 · The paper itself

Abstract

Congenital dyserythropoietic anaemia type-I (CDA-I) is a rare autosomal recessive disease characterised by ineffective erythropoiesis, haemolysis and non-haematological developmental abnormalities. Its treatment is multifactorial, including the management of anaemia, iron overload and prevention of osteoporosis. The only treatment specific to CDA-I is subcutaneous interferon alpha (IFNα) 2A. This study presents the first summary of all published cases of CDA-I patients (

Indexed as

Congenital Anaemia Networkcongenital dyserythropoietic anaemia Iinterferonpatient responsePROMS

Identifiers

PMID41598837
PMCPMC12842439

What OpenQuestion holds

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Registered trials

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Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the OpenQuestion graph.