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ArticlePharmacoEconomics2026

Mapping Health State Utility from Disease-Specific Measures in Spinal Muscular Atrophy and Paroxysmal Nocturnal Hemoglobinuria.

Ziwen Zhao et al.PubMed ↗Publisher ↗

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1 paper cites it

2026
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Full record →Abstract, authors, funding and every citing paper · PMID 41182577