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ArticlePharmaceutical research2025

Preclinical Evaluation of AAV8-R338L Gene Therapy for Hemophilia: Efficacy, Pharmacokinetics, Distribution, Excretion and Toxicity in Mouse Models and Non-human Primates.

Dehu Dou et al.PubMed ↗Publisher ↗

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2 papers cite it

2025
2026
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Full record →Abstract, authors, funding and every citing paper · PMID 41073832