ArticleNeurotherapeutics : the journal of the American Society for Experimental NeuroTherapeutics2025

Rescue of neurologic disease in mucopolysaccharidosis type II mice via AAV-mediated liver delivery of brain-penetrating iduronate-2-sulfatase.

Xiu Jin et al.PubMed ↗Full text ↗Publisher ↗

No numbers read from the abstract.