ArticleAnnals of neurology2026

AAV9-DARS2 Gene Therapy Rescues Phenotype in Leukoencephalopathy with Brainstem and Spinal Cord Involvement and Lactate Elevation Patient Cells and Neuronal Dars2 Deficient Mice.

I Garofolo et al.PubMed ↗Full text ↗Publisher ↗

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