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ArticleLife (Basel, Switzerland)2025

Efficacy and Safety of 5-Aminolevulinic Acid Hydrochloride Combined with Sodium Ferrous Citrate in Pediatric Patients with Leigh Syndrome and Central Nervous System Disorders: An Initial Exploratory Trial with a Double-Blind Placebo-Controlled Period, Followed by an Open-Label Period and a Subsequent Long-Term Administration Study.

Yuichi Abe et al.PubMed ↗Full text ↗Publisher ↗

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3 papers cite it

2025
2026
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Full record →Abstract, authors, funding and every citing paper · PMID 40868816