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ArticleMedizinische Genetik : Mitteilungsblatt des Berufsverbandes Medizinische Genetik e.V2025

Antisense oligonucleotide therapies for monogenic disorders.

Ilona Krey-Grauert et al.PubMed ↗Full text ↗Publisher ↗

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4 papers cite it

2025
2026
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Full record →Abstract, authors, funding and every citing paper · PMID 40687881