Evidence map›Paper›PMID 39969027›Full record

ArticleEinstein (Sao Paulo, Brazil)2025

Kabuki and CHARGE syndromes: overlapping symptoms and diagnostic challenges.

Bruno Pellozo Cerqueira, Elenice Andrade Milhomem, Ana Cristina Carvalho de Matos, Igor Gouveia Pietrobom, Carlos Magno Leprevost, Ita Pfeferman Heilberg

Abstract readCase Reports
In one paragraph

Article in Einstein (Sao Paulo, Brazil), 2025. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 2 papers.

0numbers the graph read from it
0cells of the map it votes in
2citing papers in PubMed
–field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

2 citing papers in PubMed.

  1. Article
  2. Article
4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

6 authors.

Bruno Pellozo CerqueiraNephrology Division, Escola Paulista de Medicina, Universidade Federal de São Paulo, São Paulo, SP, Brazil.ORCID http://orcid.org/0000-0001-7112-5511
Elenice Andrade MilhomemNephrology Division, Escola Paulista de Medicina, Universidade Federal de São Paulo, São Paulo, SP, Brazil.ORCID http://orcid.org/0000-0003-3815-1608
Ana Cristina Carvalho de MatosNephrology Division, Escola Paulista de Medicina, Universidade Federal de São Paulo, São Paulo, SP, Brazil.ORCID http://orcid.org/0000-0002-9703-3399
Igor Gouveia PietrobomNephrology Division, Escola Paulista de Medicina, Universidade Federal de São Paulo, São Paulo, SP, Brazil.ORCID http://orcid.org/0009-0000-6755-1673
Carlos Magno LeprevostSecretaria de Saúde do Paraná, Paraná, PR, Brazil.ORCID http://orcid.org/0009-0001-7310-1676
Ita Pfeferman HeilbergNephrology Division, Escola Paulista de Medicina, Universidade Federal de São Paulo, São Paulo, SP, Brazil.ORCID http://orcid.org/0000-0002-0885-5877

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

Kabuki syndrome is a rare congenital malformation with typical facial features, skeletal anomalies, delayed neuropsychomotor development and growth, and cardiac, genitourinary, gastrointestinal, endocrine, and dental anomalies. One of the main differential diagnoses is CHARGE syndrome, standing for and characterized by Coloboma of the eye, Heart defects, Atresia of the nasal choanae, Restricted intellectual development, Genitourinary malformations, and Ear anomalies. Because these syndromes have similar characteristics, distinguishing them may be challenging. A 24-year-old male patient admitted with reduced renal function had a previous phenotype-based diagnosis of CHARGE syndrome based on many characteristic clinical features. The unveiling of a hypocalcemic crisis diagnosed as primary hypoparathyroidism at the age of 15 years, which did not fit into that diagnosis, led the nephrologist to request a genetic test, which evidenced a missense variant of uncertain significance in exon 38 of the KMT2D gene. This phenotype further suggested Kabuki syndrome, ruling out CHARGE. The present report highlights the importance of genetic testing and discusses phenotype-genotype correlations, which ultimately showed that specific variants in exon 38 rendered a form of Kabuki syndrome distinct from the typical one.

Indexed as

Abnormalities, MultipleCHARGE SyndromeFaceHematologic DiseasesVestibular DiseasesDiagnosis, DifferentialDNA-Binding ProteinsHumansMaleNeoplasm ProteinsPhenotypeYoung AdultDNA-Binding ProteinsKMT2D protein, humanNeoplasm Proteins

Identifiers

PMID39969027
PMCPMC11869784

What OpenQuestion holds

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Registered trials

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Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the OpenQuestion graph.