ArticleInternational journal of molecular sciences2025

mRNA Degradation as a Therapeutic Solution for Mucopolysaccharidosis Type IIIC: Use of Antisense Oligonucleotides to Promote Downregulation of Heparan Sulfate Synthesis.

Juliana Inês Santos et al.PubMed ↗Full text ↗Publisher ↗

No numbers read from the abstract.