Evidence map›Paper›PMID 39483301›Full record

ArticleTherapeutic advances in rare disease

Neuroanatomical anomalies due to a defect in the FGF3 gene, associated with the Labyrinthine Aplasia, Microtia and Microdontia syndrome: insights from the placement of auditory brainstem implants in two siblings.

Johan H M Frijns, Roos M G S Geerders, Esther Scholing, Berit M Verbist, Radboud W Koot, Martijn J A Malessy, Peter-Paul B M Boermans, Jeroen J Briaire

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Article in Therapeutic advances in rare disease. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 2 papers.

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0cells of the map it votes in
2citing papers in PubMed
–field-weighted citation impact
1 · What the graph read from it

What it found

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The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

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Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

2 citing papers in PubMed.

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4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

8 authors.

Johan H M FrijnsDepartment of Otorhinolaryngology & HNS, Leiden University Medical Centre, P.O. Box 9600, Leiden, 2300 RC, The Netherlands.ORCID https://orcid.org/0000-0002-1180-3314
Roos M G S GeerdersDepartment of Otorhinolaryngology & HNS, Leiden University Medical Centre, Leiden, The Netherlands.ORCID https://orcid.org/0009-0003-1425-8096
Esther ScholingDepartment of Otorhinolaryngology & HNS, Leiden University Medical Centre, Leiden, The Netherlands.
Berit M VerbistDepartment of Radiology, Leiden University Medical Centre, Leiden, The Netherlands.ORCID https://orcid.org/0000-0002-1010-2583
Radboud W KootDepartment of Neurosurgery, Leiden University Medical Centre, Leiden, The Netherlands.
Martijn J A MalessyDepartment of Neurosurgery, Leiden University Medical Centre, Leiden, The Netherlands.
Peter-Paul B M BoermansDepartment of Otorhinolaryngology & HNS, Leiden University Medical Centre, Leiden, The Netherlands.
Jeroen J BriaireDepartment of Otorhinolaryngology & HNS, Leiden University Medical Centre, Leiden, The Netherlands.ORCID https://orcid.org/0000-0003-4302-817X

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

Here, we describe two congenitally deaf male siblings with the same compound heterozygotic, likely pathogenic mutations in the FGF3 gene, associated with the labyrinthine aplasia, microtia and microdontia (LAMM) syndrome. Both children had bilateral cochleovestibular aplasia, precluding cochlear implantation. The elder brother received an auditory brainstem implant (ABI) with very limited auditory responses. During the ABI-surgery of the younger subject, it was discovered that excellent auditory responses could be obtained when the electrode array was placed considerably more caudally and more medially than standard. It was observed that the foramen of Luschka, the entrance to the lateral recess of the fourth ventricle was located more caudally. In view of this observation the good auditory development of the latter child, it was decided to give the older child a contralateral ABI. Again, it turned out that the anatomy of the brainstem was abnormal with a more caudal location of the foramen of Luschka and the cochlear nucleus, and this child is showing good progress with his auditory development. It is concluded that one should be aware of the anatomical differences at the level of the brainstem when placing an ABI in children with this genetic disorder (and most likely also in the LAMM syndrome). This also underpins the need of a multidisciplinary approach with closely collaborating team members and good family guidance when diagnosing and treating children with rare deafness.

Indexed as

ABIauditory brainstem implantauditory nerve dysplasiacochleovestibular dysplasiaFGF3 geneLAMM-syndrome

Identifiers

PMID39483301
PMCPMC11526279

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Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the OpenQuestion graph.