Evidence map›Paper›PMID 38929947›Full record

ArticleJournal of clinical medicine2024

Patients' Perceptions of Nusinersen Effects According to Their Responder Status.

Charlotte Lilien, Eva Vrscaj, Gita Thapaliya, Nicolas Deconinck, Liesbeth De Waele, Tina Duong, Jana Haberlová, Markéta Kumhera, Geertrui Peirens, Lena Szabo and 5 more

Abstract read
In one paragraph

Article in Journal of clinical medicine, 2024. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 5 papers, 1 of them a synthesis that pooled it.

0numbers the graph read from it
0cells of the map it votes in
5citing papers in PubMed, 1 pooled it
–field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

5 citing papers in PubMed, 1 synthesis or guideline pooled it.

  1. Pooled it
  2. Article
  3. Observational
  4. Article
  5. Article
4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

15 authors.

Charlotte LilienMDUK Oxford Neuromuscular Centre, Department of Paediatrics, University of Oxford, Oxford OX3 9DU, UK.ORCID 0009-0001-8219-6996
Eva VrscajDivision of Child Neurology, Reference Center for Neuromuscular Diseases, Department of Paediatrics, University Hospital Liege & University of Liege, 4000 Liege, Belgium.ORCID 0000-0002-1510-0501
Gita ThapaliyaMDUK Oxford Neuromuscular Centre, Department of Paediatrics, University of Oxford, Oxford OX3 9DU, UK.
Nicolas DeconinckNMRC UZ Gent, Ghent University Hospital, 9000 Ghent, Belgium.
Liesbeth De WaeleDepartment of Paediatrics, University Hospitals Leuven, 3000 Leuven, Belgium.
Tina DuongJohn W. Day Lab, Department of Neurology and Neurological Sciences, University of Stanford, Stanford, CA 94305, USA.
Jana HaberlováDepartment of Paediatric Neurology, Second Faculty of Medicine, Charles University and Motol University Hospital, 150 06 Praha, Czech Republic.
Markéta KumheraDepartment of Paediatric Neurology, Second Faculty of Medicine, Charles University and Motol University Hospital, 150 06 Praha, Czech Republic.ORCID 0000-0003-4967-4797
Geertrui PeirensDepartment of Paediatrics, University Hospitals Leuven, 3000 Leuven, Belgium.
Lena SzaboPaediatric Center, Semmelweis University, 1083 Budapest, Hungary.
Valentine TahonNMRC UZ Gent, Ghent University Hospital, 9000 Ghent, Belgium.
Whitney J TangJohn W. Day Lab, Department of Neurology and Neurological Sciences, University of Stanford, Stanford, CA 94305, USA.
Noor BenmhammedDivision of Child Neurology, Reference Center for Neuromuscular Diseases, Department of Paediatrics, University Hospital Liege & University of Liege, 4000 Liege, Belgium.
Laurie MédardDivision of Child Neurology, Reference Center for Neuromuscular Diseases, Department of Paediatrics, University Hospital Liege & University of Liege, 4000 Liege, Belgium.
Laurent ServaisMDUK Oxford Neuromuscular Centre, Department of Paediatrics, University of Oxford, Oxford OX3 9DU, UK.ORCID 0000-0001-9270-4061

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

PubMed holds no abstract for this paper.

Indexed as

nusinersenpatient perceptionresponderspinal muscular atrophytreatment response

Identifiers

PMID38929947
PMCPMC11205004

What OpenQuestion holds

Textmetadata
LicenceCC BY
Read underepoch 390

Registered trials

None linked

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the OpenQuestion graph.