Evidence map›Paper›PMID 36944600›Full record

ArticleThe Journal of craniofacial surgery2023

Nasal Construction in Congenital Arhinia Due to Novel SMCHD1 Gene Variant.

Marie Bargiela, Janina Kueper, Arman T Serebrakian, MaKenna R Browne, Susan Brogna, Zachary S Peacock, Branko Bojovic, Natalie D Shaw, Eric C Liao

Open access · greenAbstract read
In one paragraph

Article in The Journal of craniofacial surgery, 2023. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 1 paper.

0numbers the graph read from it
0cells of the map it votes in
1citing papers in PubMed
1.4field-weighted citation impact, top 18% of its field
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

1 citing paper in PubMed, 5 citations in OpenAlex.

  1. Review
4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

9 authors at 4 institutions in 2 countries.

Marie BargielaDivision of Plastic and Reconstructive Surgery, Massachusetts General Hospital, Harvard Medical School.
Janina KueperDivision of Plastic and Reconstructive Surgery, Massachusetts General Hospital, Harvard Medical School.
Arman T SerebrakianDivision of Plastic and Reconstructive Surgery, Massachusetts General Hospital, Harvard Medical School.
MaKenna R BrownePediatric Neuroendocrinology Group, Clinical Research Branch, National Institute of Environmental Health Sciences, Research Triangle Park, NC.
Susan BrognaShriners Hospital for Children, Boston, MA.
Zachary S PeacockShriners Hospital for Children, Boston, MA.
Branko BojovicDivision of Plastic and Reconstructive Surgery, Massachusetts General Hospital, Harvard Medical School.
Natalie D ShawPediatric Neuroendocrinology Group, Clinical Research Branch, National Institute of Environmental Health Sciences, Research Triangle Park, NC.
Eric C LiaoDivision of Plastic and Reconstructive Surgery, Massachusetts General Hospital, Harvard Medical School.
Shriners Hospitals for Children - Boston · USNational Institute of Environmental Health Sciences · USMassachusetts General Hospital · USUniversity of Bonn · DE

Funding

Program in Clinical Research, Clinical Support Services and Clinical TrainingZIDES102465 · NIEHS · NATIONAL INSTITUTE OF ENVIRONMENTAL HEALTH SCIENCES · PI KIRSCHNER, LAWRENCE · 2009 to 2025
$84.7M
RAPID GENE DISCOVERYP01GM061354 · NIGMS · BRIGHAM AND WOMEN'S HOSPITAL · PI MORTON, CYNTHIA CASSON · 2001 to 2019
$24.3M
Investigation of the genetic architecture and phenotypic spectrum of Bosma arhinia microphthalmia syndromeZIAES103327 · NIEHS · NATIONAL INSTITUTE OF ENVIRONMENTAL HEALTH SCIENCES · PI SHAW, NATALIE · 2017 to 2025
$15.5M
Rapid Identification and Validation of Human Craniofacial Development GenesU01DE024443 · NIDCR · BRIGHAM AND WOMEN'S HOSPITAL · PI MAAS, RICHARD L · 2014 to 2018
$2.9M
Intramural NIH HHS ZIA ES103327Intramural NIH HHS ZID ES102465NIDCR NIH HHS U01 DE024443NIGMS NIH HHS P01 GM061354
6 · The paper itself

Abstract

Arhinia, or congenital absence of the nose, is an exceedingly rare anomaly caused by pathogenic variants in the gene SMCHD1 . Arhinia exhibits unique reconstructive challenges, as the midface is deficient in skeletal and soft tissue structures. The authors present 2 related patients with arhinia who harbor a novel SMCHD1 gene variant and illustrate their surgical midface and nasal construction. Targeted sequencing was carried out on DNA samples from the 2 affected patients, 1 anosmic and 1 healthy parent, to identify variants in exons 3 to 13 of SMCHD1 . The affected patients and anosmic parent were found to have a novel SMCHD1 gene variant p.E473V. A staged surgical approach was applied. First, both patients underwent a LeFort II osteotomy and distraction osteogenesis to improve the projection of the midfacial segment, followed by tissue expansion of the forehead, and nasal construction with a forehead flap that was placed over a costochondral framework derived from rib cartilage. The novel gene variant could guide future investigations on genetic pathways and molecular processes that underly the physiological and pathologic development of the nose. Further investigations on the variable expressivity ranging from anosmia to arhinia could improve clinical genetic screens for risk stratification of individuals with anosmia on passing on arhinia to their children. Due to the exceptional rarity and complexity of congenital arhinia, most surgical approaches are developed on a single-case basis. This case series, albeit limited to 2 cases, is the largest pedigree of such cases in the literature. It highlights key principles of a staged approach to nasal construction in arhinia and discusses nuances and improvements learned between both patients. It subsequently offers an optimized guide to this surgical strategy.

Indexed as

AnosmiaPlastic Surgery ProceduresChildChromosomal Proteins, Non-HistoneCongenital AbnormalitiesHumansNosePedigreeChromosomal Proteins, Non-HistoneSMCHD1 protein, human

Identifiers

PMID36944600
PMCPMC10802859
OpenAlexW4353015896

What OpenQuestion holds

Textmetadata
LicenceTDM
Read underepoch 390

Registered trials

None linked

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the OpenQuestion graph.