ArticleDisease models & mechanisms2022
The predictive value of models of neuromuscular disorders to potentiate clinical translation.
Article in Disease models & mechanisms, 2022. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 3 papers.
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The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.
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Who cites it
3 citing papers in PubMed.
- Supporting the translation of multiscale research in rare disease.Disease models & mechanisms · 2023Article
- Impactful in disease research: a DMM year in review.Disease models & mechanisms · 2023Article
- Sharing resources to advance translational research.Disease models & mechanisms · 2022Article
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1 author.
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Abstract
Neuromuscular disorders (NMDs) are a heterogenous group of rare inherited diseases that compromise the function of peripheral nerves and/or muscles. With limited treatment options available, there is a growing need to design effective preclinical studies that can lead to greater success in clinical trials for novel therapeutics. Here, I discuss recent advances in modelling NMDs to improve preclinical studies as well as two articles from this issue that work in parallel to enable a deeper understanding of a particularly rare NMD, known as X-linked myotubular myopathy.
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Registered trials
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