Evidence map›Paper›PMID 35782601›Full record

ArticleMolecular genetics and metabolism reports2022

Clinical characteristics and effects of enzyme replacement therapy with elosulfase alfa in Korean patients with mucopolysaccharidosis type IVA.

Seung Hoon Lee, Hwa Young Kim, Tae-Joon Cho, Hyoungmin Kim, Jung Min Ko

Open access · goldAbstract read
PubMed Full text at PMC Publisher
In one paragraph

Article in Molecular genetics and metabolism reports, 2022. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 3 papers.

0numbers the graph read from it
0cells of the map it votes in
3citing papers in PubMed
0.2field-weighted citation impact, top 49% of its field
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

3 citing papers in PubMed, 2 citations in OpenAlex.

  1. Article
  2. Article
  3. Mucopolysaccharidosis IVA: Current Disease Models and Drawbacks.International journal of molecular sciences · 2023
    Review
4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

5 authors at 1 institution in 1 country.

Seung Hoon LeeDepartment of Pediatrics, Seoul National University College of Medicine, Republic of Korea.
Hwa Young KimDepartment of Pediatrics, Seoul National University College of Medicine, Republic of Korea.
Tae-Joon ChoDepartment of Orthopaedics, Seoul National University College of Medicine, Republic of Korea.
Hyoungmin KimDepartment of Orthopaedics, Seoul National University College of Medicine, Republic of Korea.
Jung Min KoDepartment of Pediatrics, Seoul National University College of Medicine, Republic of Korea.
Seoul National University · KR

Funding

No grant is acknowledged in the PubMed record.

6 · The paper itself

Abstract

Mucopolysaccharidosis type IVA (MPS IVA) is a rare autosomal recessive disorder caused by a deficiency in

Indexed as

6MWT, 6-min walk testElosulfase alfaEnzyme replacement therapyERT, enzyme replacement therapyFIM, (Functional Independence Measure)GAGs, glycosaminoglycansGALNS, N-acetylgalactosamine-6-sulfataseKoreanMorquio A syndromeMPS IVA, Mucopolysaccharidosis type IVAMucopolysaccharidosis type IVASDS_K, standard deviation score for height based on Korean National Growth ChartsSDS_M, standard deviation score for height based on untreated MPS IVA growth referenceSDS, standard deviation scoreTreatment outcome

Identifiers

PMID35782601
PMCPMC9248211
OpenAlexW4223907561

What OpenQuestion holds

Textmetadata
LicenceCC BY-NC-ND
Read underepoch 390

Registered trials

None linked

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the OpenQuestion graph.