ArticleMolecular therapy : the journal of the American Society of Gene Therapy2021
Eliminating Panglossian thinking in development of AAV therapeutics.
Article in Molecular therapy : the journal of the American Society of Gene Therapy, 2021. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 9 papers.
What it found
Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.
The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.
The trial behind it
Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.
Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.
Who cites it
9 citing papers in PubMed.
- Why is the uptake of gene therapy in hemophilia less than expected?Research and practice in thrombosis and haemostasis · 2025Article
- Two gene therapies for hemophilia available: Now what?Molecular therapy : the journal of the American Society of Gene Therapy · 2023Article
- Ectopic clotting factor VIII expression and misfolding in hepatocytes as a cause for hepatocellular carcinoma.Molecular therapy : the journal of the American Society of Gene Therapy · 2022Article
- IL-15 blockade and rapamycin rescue multifactorial loss of factor VIII from AAV-transduced hepatocytes in hemophilia A mice.Molecular therapy : the journal of the American Society of Gene Therapy · 2022Article
- Transient expression of factor VIII and a chronic high-fat diet induces ER stress and late hepatocyte oncogenesis.Molecular therapy : the journal of the American Society of Gene Therapy · 2022Article
- First conditional marketing authorization approval in the European Union for hemophilia "A" gene therapy.Molecular therapy : the journal of the American Society of Gene Therapy · 2022Article
- Gene therapy - are we ready now?Haemophilia : the official journal of the World Federation of Hemophilia · 2022Article
- Treatment-induced hemophilic thrombosis?Molecular therapy : the journal of the American Society of Gene Therapy · 2022Article
- The Hemophilia Gene Therapy Patient Journey: Questions and Answers for Shared Decision-Making.Patient preference and adherence · 2022Article
Corrections and comments
PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.
Authors and funding
6 authors.
Funding
No grant is acknowledged in the PubMed record.
Abstract
PubMed holds no abstract for this paper.
Indexed as
Identifiers
What OpenQuestion holds
Registered trials
Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the OpenQuestion graph.