ArticleMolecular therapy : the journal of the American Society of Gene Therapy2021

DUX4 Transcript Knockdown with Antisense 2'-O-Methoxyethyl Gapmers for the Treatment of Facioscapulohumeral Muscular Dystrophy.

Kenji Rowel Q Lim et al.PubMed ↗Full text ↗Publisher ↗

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