TrialClinical pharmacokinetics2021
Pharmacokinetic and Pharmacodynamic Properties of Cemdisiran, an RNAi Therapeutic Targeting Complement Component 5, in Healthy Subjects and Patients with Paroxysmal Nocturnal Hemoglobinuria.
Prajakta Badri et al.PubMed ↗Full text ↗Publisher ↗
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