TrialMolecular therapy : the journal of the American Society of Gene Therapy2021
A Phase 2/3 Trial of Pabinafusp Alfa, IDS Fused with Anti-Human Transferrin Receptor Antibody, Targeting Neurodegeneration in MPS-II.
Torayuki Okuyama et al.PubMed ↗Full text ↗Publisher ↗
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