Evidence map›Paper›PMID 32623069›Full record

ArticleThe Journal of allergy and clinical immunology2020

Gene therapy for Wiskott-Aldrich syndrome: History, new vectors, future directions.

Francesca Ferrua, Francesco Marangoni, Alessandro Aiuti, Maria Grazia Roncarolo

Abstract readEditorial
In one paragraph

Article in The Journal of allergy and clinical immunology, 2020. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 22 papers.

0numbers the graph read from it
0cells of the map it votes in
22citing papers in PubMed
–field-weighted citation impact
1 · What the graph read from it

What it found

Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.

The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.

2 · The registry

The trial behind it

Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.

Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.

3 · Its place in the literature

Who cites it

22 citing papers in PubMed.

  1. Review
  2. Article
  3. Review
  4. Article
  5. Advancing Precision Medicine: Recent Innovations in Gene Editing Technologies.Advanced science (Weinheim, Baden-Wurttemberg, Germany) · 2025
    Review
  6. Article
  7. Review
  8. [Advances in gene therapy for inborn errors of immunity].Zhongguo dang dai er ke za zhi = Chinese journal of contemporary pediatrics · 2024
    Review
  9. Article
  10. Article
  11. Autoimmunity in Primary Immunodeficiencies (PID).Clinical reviews in allergy & immunology · 2023
    Review
  12. Article
  13. Review
  14. Review
  15. Gene therapy for Whiskott-Aldrich syndrome: The latest news.Clinical and translational medicine · 2022
    Article
  16. Article
  17. Update on Clinical Ex Vivo Hematopoietic Stem Cell Gene Therapy for Inherited Monogenic Diseases.Molecular therapy : the journal of the American Society of Gene Therapy · 2021
    Review
  18. Review
  19. Review
  20. Article
4 · The record

Corrections and comments

PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.

5 · Who and what money

Authors and funding

4 authors.

Francesca FerruaSan Raffaele Telethon Institute for Gene Therapy (SR-Tiget) and Pediatric Immunohematology and Bone Marrow Transplantation Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy.
Francesco MarangoniDepartment of Physiology and Biophysics and Institute for Immunology, University of California, Irvine, Calif.
Alessandro AiutiSan Raffaele Telethon Institute for Gene Therapy (SR-Tiget) and Pediatric Immunohematology and Bone Marrow Transplantation Unit, IRCCS San Raffaele Scientific Institute, Milan, Italy; Vita-Salute San Raffaele University, Milan, Italy.
Maria Grazia RoncaroloDivision of Stem Cell Transplantation and Regenerative Medicine, Department of Pediatrics and Institute for Stem Cell Biology and Regenerative Medicine, Stanford University School of Medicine, Stanford, Calif. Electronic address: mg1@stanford.edu.

Funding

Mechanisms of Macrophage Functional Switch during Skin RepairR21AR072849 · NIAMS · UNIVERSITY OF CALIFORNIA-IRVINE · PI MARANGONI, FRANCESCO · 2019 to 2020
$379k
NIAMS NIH HHS R21 AR072849
6 · The paper itself

Abstract

PubMed holds no abstract for this paper.

Indexed as

Genetic TherapyGenetic VectorsHematopoietic Stem CellsHumansMaleTransplantation ConditioningWiskott-Aldrich SyndromeGene therapyhematopoietic stem/progenitor celllentiviral vectorreduced-intensity conditioningWiskott-Aldrich syndrome

Identifiers

PMID32623069
PMCPMC7453879

What OpenQuestion holds

Textmetadata
LicenceTDM
Read underepoch 390

Registered trials

None linked

Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the OpenQuestion graph.