ArticleHuman molecular genetics2020

Correction of amyotrophic lateral sclerosis related phenotypes in induced pluripotent stem cell-derived motor neurons carrying a hexanucleotide expansion mutation in C9orf72 by CRISPR/Cas9 genome editing using homology-directed repair.

Nidaa A Ababneh et al.PubMed ↗Full text ↗Publisher ↗

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