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ArticleAdvanced science (Weinheim, Baden-Wurttemberg, Germany)2020

Dual Supramolecular Nanoparticle Vectors Enable CRISPR/Cas9-Mediated Knockin of Retinoschisin 1 Gene-A Potential Nonviral Therapeutic Solution for X-Linked Juvenile Retinoschisis.

Shih-Jie Chou et al.PubMed ↗Full text ↗Publisher ↗

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