ArticleJournal of postgraduate medicine
Enzyme replacement therapy in India: Lessons and insights.
Article in Journal of postgraduate medicine. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 12 papers.
What it found
Each row is one number read from the abstract, on the scale the paper reported it, with its interval. Left of the dashed line favours the treatment, right favours the comparator. Under each row is the sentence it came from. New to these charts? A ten-minute tutorial.
The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.
The trial behind it
Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.
Neither the registry nor the abstract names a trial number. If this is a trial report, that itself is worth knowing.
Who cites it
12 citing papers in PubMed.
- Long-Term Outcomes of Enzyme Replacement Therapy in Indian Patients with Gaucher Disease - A Multicentric Study.Indian journal of pediatrics · 2026Article
- Plant molecular farming: a promising frontier for orphan drug production.Biotechnology letters · 2025Review
- Economic Burden of Gaucher Disease at a Tertiary Care Public Hospital in Mumbai.Indian journal of pediatrics · 2024Article
- Rare genetic disorders in India: Current status, challenges, and CRISPR-based therapy.Journal of biosciences · 2024Review
- Enhancing access to treatment for Gaucher disease in India: The need for indigenous manufacturing.Journal of biosciences · 2024Article
- Lysosomal storage disorders: from biology to the clinic with reference to India.The Lancet regional health. Southeast Asia · 2023Review
- Transformative effect of a Humanitarian Program for individuals affected by rare diseases: building support systems and creating local expertise.Orphanet journal of rare diseases · 2022Review
- Challenges in Chronic Genetic Disorders: Lessons From the COVID-19 Pandemic.Indian pediatrics · 2021Article
- Spectrum of Lysosomal Storage Disorders at Tertiary Centre: Retrospective Case-Record Analysis.Journal of pediatric genetics · 2020Article
- Genomics of rare genetic diseases-experiences from India.Human genomics · 2019Review
- The role of patient organizations in the rare disease ecosystem in India: an interview based study.Orphanet journal of rare diseases · 2019Article
- Advances in orphan drug development: Time to change the status and stereotype.Perspectives in clinical researchReview
Corrections and comments
PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.
Authors and funding
2 authors.
Funding
No grant is acknowledged in the PubMed record.
Abstract
PubMed holds no abstract for this paper.
Indexed as
Identifiers
What OpenQuestion holds
Registered trials
Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the OpenQuestion graph.