TrialGenetics in medicine : official journal of the American College of Medical Genetics2018

Efficacy, safety profile, and immunogenicity of alglucosidase alfa produced at the 4,000-liter scale in US children and adolescents with Pompe disease: ADVANCE, a phase IV, open-label, prospective study.

Si Houn Hahn et al.PubMed ↗Publisher ↗

No numbers read from the abstract.