ArticleMolecular genetics and metabolism reports2017

Letter to the Editors: Concerning "Divergent clinical outcomes of alphaglucosidase enzyme replacement therapy in two siblings with infantile-onset Pompe disease treated in the symptomatic or pre-symptomatic state" by Takashi M et al.

Rita Ortolano et al.PubMed ↗Full text ↗Publisher ↗

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