ArticleThe New England journal of medicine2015
Lysosomal Acid Lipase Deficiency--A New Therapy for a Genetic Lipid Disease.
Article in The New England journal of medicine, 2015. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 15 papers.
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The trial behind it
Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.
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Who cites it
15 citing papers in PubMed, 36 citations in OpenAlex.
- Sebelipase alfa for lysosomal acid lipase deficiency: 5-year treatment experience from a phase 2 open-label extension study.Liver international : official journal of the International Association for the Study of the Liver · 2020Trial
- Liver-specific gene therapy based on self-complementary adeno-associated virus for lysosomal acid lipase deficiency.Frontiers in pharmacology · 2026Article
- Sebelipase Alfa Improves Aminotransferase Levels in Lysosomal Acid Lipase Deficiency: Data From an International Registry.Liver international : official journal of the International Association for the Study of the Liver · 2025Observational
- Screening for Lysosomal Acid Lipase Deficiency in a Lipid Clinic.Arquivos brasileiros de cardiologia · 2025Article
- Identification of key genes associated with acute myocardial infarction using WGCNA and two-sample mendelian randomization study.PloS one · 2024Article
- The Emerging Battle: Lysosomal Acid Lipase Deficiency vs Familial Hypercholesterolemia in Children.ACG case reports journal · 2021Article
- MicroRNA‑494 suppresses hypoxia/reoxygenation‑induced cardiomyocyte apoptosis and autophagy via the PI3K/AKT/mTOR signaling pathway by targeting SIRT1.Molecular medicine reports · 2020Article
- Lysosomal Acid Lipase Is Required for Donor T Cells to Induce Graft-versus-Host Disease.Cell reports · 2020Article
- Crystal structure of human lysosomal acid lipase and its implications in cholesteryl ester storage disease.Journal of lipid research · 2020Article
- Hepatocyte-specific lysosomal acid lipase deficiency protects mice from diet-induced obesity but promotes hepatic inflammation.Biochimica et biophysica acta. Molecular and cell biology of lipids · 2019Article
- Hepatosteatosis from Lysosomal Acid Lipase Deficiency.Journal of gastrointestinal surgery : official journal of the Society for Surgery of the Alimentary Tract · 2019Article
- Lysosomal Acid Lipase Deficiency, a Rare Pathology: The First Pediatric Patient Reported in Colombia.The American journal of case reports · 2018Article
- Different Covalent Immobilizations Modulate Lipase Activities of Hypocrea pseudokoningii.Molecules (Basel, Switzerland) · 2017Article
- The Arf-like GTPase Arl8b is essential for three-dimensional invasive growth of prostate cancer in vitro and xenograft formation and growth in vivo.Oncotarget · 2016Article
- Dyslipidaemia: Lysosomal acid lipase deficiency-a cautious leap forward.Nature reviews. Endocrinology · 2015Article
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1 author at 1 institution in 1 country.
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Registered trials
Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the OpenQuestion graph.