ArticleThe European journal of health economics : HEPAC : health economics in prevention and care2015
Rare is frequent and frequent is costly: rare diseases as a challenge for health care systems.
Article in The European journal of health economics : HEPAC : health economics in prevention and care, 2015. The graph could read no effect estimate from its abstract, so it casts no vote on the map. Cited by 26 papers, 1 of them a synthesis that pooled it.
What it found
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The abstract states no effect estimate the extractor could read, or names no intervention and outcome on the map, so this paper lights no cell and moves no belief. It is still indexed, cited and linked below.
The trial behind it
Trials whose registry record cites this paper, or whose number appears in the abstract. A trial that started after this paper was published is citing it as background, not reporting it.
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Who cites it
26 citing papers in PubMed, 1 synthesis or guideline pooled it.
- Employment and work ability in individuals living with rare diseases: a systematic literature review.Orphanet journal of rare diseases · 2025Pooled it
- Genomic Strategies in Pediatric Care: Addressing Rare Diseases in Children.Children (Basel, Switzerland) · 2026Review
- Financial Burden in Adults With Chronic Illness in Switzerland: A Secondary Analysis of Qualitative Interviews Using Natural Language Processing and Topic Modeling.JMIR formative research · 2026Article
- Levels and correlates of pandemic anxiety in people living with rare diseases: a cross-sectional analysis using a structural equation model.Orphanet journal of rare diseases · 2026Article
- A structured approach for identifying disease analogs for pulmonary arterial hypertension.Journal of managed care & specialty pharmacy · 2025Article
- Experiences and Needs Regarding Information Provision in Children With Haemophilia: A Qualitative Study on Caregivers' and Healthcare Providers' Perspectives.Haemophilia : the official journal of the World Federation of Hemophilia · 2025Article
- Article
- Latent profiles and predictors of barriers to care in Swiss children and adolescents with rare diseases.Journal of pediatric psychology · 2024Article
- Rare diseases in Tanzania: a National Call for Action to address policy and urgent needs of individuals with rare diseases.Orphanet journal of rare diseases · 2022Article
- Family caregivers of rare disease: A survey on health-related quality of life in family caregivers for Gaucher disease patients in China.Molecular genetics & genomic medicine · 2021Article
- Cost-of-illness studies in rare diseases: a scoping review.Orphanet journal of rare diseases · 2021Article
- How are patients with rare diseases and their carers in the UK impacted by the way care is coordinated? An exploratory qualitative interview study.Orphanet journal of rare diseases · 2021Article
- Genome Editing in iPSC-Based Neural Systems: From Disease Models to Future Therapeutic Strategies.Frontiers in genome editing · 2021Review
- Dynamics of patents, orphan drug designation, licensing, and revenues from drugs for rare diseases: The market expansion of eculizumab.PloS one · 2021Article
- Cost-effectiveness analysis of using the TBX6-associated congenital scoliosis risk score (TACScore) in genetic diagnosis of congenital scoliosis.Orphanet journal of rare diseases · 2020Article
- Identifying disease-causing mutations in genomes of single patients by computational approaches.Human genetics · 2020Review
- Network for Therapy in Rare Epilepsies (NETRE): Lessons From the Past 15 Years.Frontiers in neurology · 2020Review
- Public spending on orphan medicines: a review of the literature.Journal of pharmaceutical policy and practice · 2020Article
- RD-RAP: beyond rare disease patient registries, devising a comprehensive data and analytic framework.Orphanet journal of rare diseases · 2019Article
- Personalized Medicine and Pay for Performance: Should Pharmaceutical Firms be Fully Penalized when Treatment Fails?PharmacoEconomics · 2018Article
Corrections and comments
PubMed lists nothing against this paper. Absence here is not a guarantee, only a check that was made.
Authors and funding
2 authors.
Funding
No grant is acknowledged in the PubMed record.
Abstract
PubMed holds no abstract for this paper.
Indexed as
Identifiers
25355295What OpenQuestion holds
Registered trials
Read under generation 80e0d062 · epoch 390. Bibliography from PubMed, PubMed Central and OpenAlex; grants from NIH RePORTER; trial links from ClinicalTrials.gov; estimates, votes and beliefs from the OpenQuestion graph.